Etiology
McNally P,
Singh A,
McColley SA,
Davies JC,
Higgins M,
Liu M,
Lu J,
Rodriguez-Romero V,
Shih JL,
Rosenfeld M;
VX15-770-124 Study Group
J Cyst Fibros
2024 May;23(3):429-435.
Epub 2024 Apr 4
doi: 10.1016/j.jcf.2024.03.012.
PMID: 38580563
Durfey SL,
Pipavath S,
Li A,
Vo AT,
Ratjen A,
Carter S,
Morgan SJ,
Radey MC,
Grogan B,
Salipante SJ,
Welsh MJ,
Stoltz DA,
Goss CH,
McKone EF,
Singh PK
mBio
2021 Dec 21;12(6):e0314821.
Epub 2021 Dec 14
doi: 10.1128/mbio.03148-21.
PMID: 34903059Free PMC Article
Dave K,
Dobra R,
Scott S,
Saunders C,
Matthews J,
Simmonds NJ,
Davies JC
Pediatr Pulmonol
2021 Feb;56 Suppl 1:S79-S89.
doi: 10.1002/ppul.24968.
PMID: 33434412
Schechter MS
Paediatr Respir Rev
2017 Sep;24:24-28.
Epub 2017 Jun 12
doi: 10.1016/j.prrv.2017.06.002.
PMID: 28712576
Konstan MW,
Plant BJ,
Elborn JS,
Rodriguez S,
Munck A,
Ahrens R,
Johnson C
Pediatr Pulmonol
2015 May;50(5):447-55.
Epub 2015 Mar 9
doi: 10.1002/ppul.23173.
PMID: 25755212
Diagnosis
Dave K,
Dobra R,
Scott S,
Saunders C,
Matthews J,
Simmonds NJ,
Davies JC
Pediatr Pulmonol
2021 Feb;56 Suppl 1:S79-S89.
doi: 10.1002/ppul.24968.
PMID: 33434412
Donaldson SH,
Pilewski JM,
Griese M,
Cooke J,
Viswanathan L,
Tullis E,
Davies JC,
Lekstrom-Himes JA,
Wang LT;
VX11-661-101 Study Group
Am J Respir Crit Care Med
2018 Jan 15;197(2):214-224.
doi: 10.1164/rccm.201704-0717OC.
PMID: 28930490Free PMC Article
Ratjen F,
Hug C,
Marigowda G,
Tian S,
Huang X,
Stanojevic S,
Milla CE,
Robinson PD,
Waltz D,
Davies JC;
VX14-809-109 investigator group
Lancet Respir Med
2017 Jul;5(7):557-567.
Epub 2017 Jun 9
doi: 10.1016/S2213-2600(17)30215-1.
PMID: 28606620
Quintana-Gallego E,
Delgado-Pecellín I,
Calero Acuña C
Arch Bronconeumol
2014 Apr;50(4):146-50.
Epub 2013 Oct 2
doi: 10.1016/j.arbres.2013.07.013.
PMID: 24095197
De Boeck K,
Kent L,
Davies J,
Derichs N,
Amaral M,
Rowe SM,
Middleton P,
de Jonge H,
Bronsveld I,
Wilschanski M,
Melotti P,
Danner-Boucher I,
Boerner S,
Fajac I,
Southern K,
de Nooijer RA,
Bot A,
de Rijke Y,
de Wachter E,
Leal T,
Vermeulen F,
Hug MJ,
Rault G,
Nguyen-Khoa T,
Barreto C,
Proesmans M,
Sermet-Gaudelus I;
European Cystic Fibrosis Society Clinical Trial Network Standardisation Committee
Eur Respir J
2013 Jan;41(1):203-16.
Epub 2012 Aug 9
doi: 10.1183/09031936.00057512.
PMID: 22878883
Therapy
Sadras I,
Kerem E,
Livnat G,
Sarouk I,
Breuer O,
Reiter J,
Gileles-Hillel A,
Inbar O,
Cohen M,
Gamliel A,
Stanleigh N,
Gunawardena T,
Bartlett C,
Gonska T,
Moraes T,
Eckford PDW,
Bear CE,
Ratjen F,
Kerem B,
Wilschanski M,
Shteinberg M,
Cohen-Cymberknoh M
J Cyst Fibros
2023 Nov;22(6):1062-1069.
Epub 2023 Jun 16
doi: 10.1016/j.jcf.2023.06.001.
PMID: 37331863
Durfey SL,
Pipavath S,
Li A,
Vo AT,
Ratjen A,
Carter S,
Morgan SJ,
Radey MC,
Grogan B,
Salipante SJ,
Welsh MJ,
Stoltz DA,
Goss CH,
McKone EF,
Singh PK
mBio
2021 Dec 21;12(6):e0314821.
Epub 2021 Dec 14
doi: 10.1128/mbio.03148-21.
PMID: 34903059Free PMC Article
Dave K,
Dobra R,
Scott S,
Saunders C,
Matthews J,
Simmonds NJ,
Davies JC
Pediatr Pulmonol
2021 Feb;56 Suppl 1:S79-S89.
doi: 10.1002/ppul.24968.
PMID: 33434412
Xia X
Cell Biol Toxicol
2020 Dec;36(6):591-602.
Epub 2020 Aug 11
doi: 10.1007/s10565-020-09552-2.
PMID: 32780246Free PMC Article
Konstan MW,
Plant BJ,
Elborn JS,
Rodriguez S,
Munck A,
Ahrens R,
Johnson C
Pediatr Pulmonol
2015 May;50(5):447-55.
Epub 2015 Mar 9
doi: 10.1002/ppul.23173.
PMID: 25755212
Prognosis
McNally P,
Singh A,
McColley SA,
Davies JC,
Higgins M,
Liu M,
Lu J,
Rodriguez-Romero V,
Shih JL,
Rosenfeld M;
VX15-770-124 Study Group
J Cyst Fibros
2024 May;23(3):429-435.
Epub 2024 Apr 4
doi: 10.1016/j.jcf.2024.03.012.
PMID: 38580563
Durfey SL,
Pipavath S,
Li A,
Vo AT,
Ratjen A,
Carter S,
Morgan SJ,
Radey MC,
Grogan B,
Salipante SJ,
Welsh MJ,
Stoltz DA,
Goss CH,
McKone EF,
Singh PK
mBio
2021 Dec 21;12(6):e0314821.
Epub 2021 Dec 14
doi: 10.1128/mbio.03148-21.
PMID: 34903059Free PMC Article
Xia X
Cell Biol Toxicol
2020 Dec;36(6):591-602.
Epub 2020 Aug 11
doi: 10.1007/s10565-020-09552-2.
PMID: 32780246Free PMC Article
Donaldson SH,
Pilewski JM,
Griese M,
Cooke J,
Viswanathan L,
Tullis E,
Davies JC,
Lekstrom-Himes JA,
Wang LT;
VX11-661-101 Study Group
Am J Respir Crit Care Med
2018 Jan 15;197(2):214-224.
doi: 10.1164/rccm.201704-0717OC.
PMID: 28930490Free PMC Article
Konstan MW,
Plant BJ,
Elborn JS,
Rodriguez S,
Munck A,
Ahrens R,
Johnson C
Pediatr Pulmonol
2015 May;50(5):447-55.
Epub 2015 Mar 9
doi: 10.1002/ppul.23173.
PMID: 25755212
Clinical prediction guides
Durfey SL,
Pipavath S,
Li A,
Vo AT,
Ratjen A,
Carter S,
Morgan SJ,
Radey MC,
Grogan B,
Salipante SJ,
Welsh MJ,
Stoltz DA,
Goss CH,
McKone EF,
Singh PK
mBio
2021 Dec 21;12(6):e0314821.
Epub 2021 Dec 14
doi: 10.1128/mbio.03148-21.
PMID: 34903059Free PMC Article
Burgel PR,
Durieu I,
Chiron R,
Mely L,
Prevotat A,
Murris-Espin M,
Porzio M,
Abely M,
Reix P,
Marguet C,
Macey J,
Sermet-Gaudelus I,
Corvol H,
Bui S,
Biouhee T,
Hubert D,
Munck A,
Lemonnier L,
Dehillotte C,
Silva JD,
Paillasseur JL,
Martin C;
French Cystic Fibrosis Reference Network study group
J Cyst Fibros
2021 Mar;20(2):220-227.
Epub 2020 Jun 24
doi: 10.1016/j.jcf.2020.06.012.
PMID: 32591294
Xia X
Cell Biol Toxicol
2020 Dec;36(6):591-602.
Epub 2020 Aug 11
doi: 10.1007/s10565-020-09552-2.
PMID: 32780246Free PMC Article
Schechter MS
Paediatr Respir Rev
2017 Sep;24:24-28.
Epub 2017 Jun 12
doi: 10.1016/j.prrv.2017.06.002.
PMID: 28712576
Konstan MW,
Plant BJ,
Elborn JS,
Rodriguez S,
Munck A,
Ahrens R,
Johnson C
Pediatr Pulmonol
2015 May;50(5):447-55.
Epub 2015 Mar 9
doi: 10.1002/ppul.23173.
PMID: 25755212