U.S. flag

An official website of the United States government

Format

Send to:

Choose Destination

dystrophia

MedGen UID:
894002
Concept ID:
CN239855
Disease or Syndrome

Professional guidelines

PubMed

Ait Benichou S, Jauvin D, De Serres-Bérard T, Pierre M, Ling KK, Bennett CF, Rigo F, Gourdon G, Chahine M, Puymirat J
Gene Ther 2022 Dec;29(12):698-709. Epub 2022 Jan 25 doi: 10.1038/s41434-022-00316-7. PMID: 35075265Free PMC Article
Marsh S, Hanson B, Wood MJA, Varela MA, Roberts TC
Mol Ther 2020 Dec 2;28(12):2527-2539. Epub 2020 Oct 14 doi: 10.1016/j.ymthe.2020.10.005. PMID: 33171139Free PMC Article
Kelly AM
Curr Opin Pulm Med 2009 Jul;15(4):376-9. doi: 10.1097/MCP.0b013e32832ae314. PMID: 19373088

Recent clinical studies

Etiology

Weiss JS, Rapuano CJ, Seitz B, Busin M, Kivelä TT, Bouheraoua N, Bredrup C, Nischal KK, Chawla H, Borderie V, Kenyon KR, Kim EK, Møller HU, Munier FL, Berger T, Lisch W
Cornea 2024 Apr 1;43(4):466-527. Epub 2024 Feb 12 doi: 10.1097/ICO.0000000000003420. PMID: 38359414Free PMC Article
Veyckemans F, Scholtes JL
Paediatr Anaesth 2013 Sep;23(9):794-803. Epub 2013 Feb 5 doi: 10.1111/pan.12120. PMID: 23384336
Vainzof M, Ayub-Guerrieri D, Onofre PC, Martins PC, Lopes VF, Zilberztajn D, Maia LS, Sell K, Yamamoto LU
J Mol Neurosci 2008 Mar;34(3):241-8. Epub 2008 Jan 18 doi: 10.1007/s12031-007-9023-9. PMID: 18202836
Lambrecht JT, Kreusch T
Cleft Palate Craniofac J 1997 Jul;34(4):342-50. doi: 10.1597/1545-1569_1997_034_0341_eyocpf_2.3.co_2. PMID: 9257026
Höweler CJ, Busch HF, Bernini LF, van Loghem E, Meera Khan P, Nijenhuis LE
Brain 1980 Sep;103(3):497-513. doi: 10.1093/brain/103.3.497. PMID: 7417778

Diagnosis

Weiss JS, Rapuano CJ, Seitz B, Busin M, Kivelä TT, Bouheraoua N, Bredrup C, Nischal KK, Chawla H, Borderie V, Kenyon KR, Kim EK, Møller HU, Munier FL, Berger T, Lisch W
Cornea 2024 Apr 1;43(4):466-527. Epub 2024 Feb 12 doi: 10.1097/ICO.0000000000003420. PMID: 38359414Free PMC Article
Weiss JS, Møller HU, Aldave AJ, Seitz B, Bredrup C, Kivelä T, Munier FL, Rapuano CJ, Nischal KK, Kim EK, Sutphin J, Busin M, Labbé A, Kenyon KR, Kinoshita S, Lisch W
Cornea 2015 Feb;34(2):117-59. doi: 10.1097/ICO.0000000000000307. PMID: 25564336
Thornton CA
Neurol Clin 2014 Aug;32(3):705-19, viii. Epub 2014 Jun 6 doi: 10.1016/j.ncl.2014.04.011. PMID: 25037086Free PMC Article
Mankodi A
Neurol India 2008 Jul-Sep;56(3):298-304. doi: 10.4103/0028-3886.43448. PMID: 18974556
Thornton C
Semin Neurol 1999;19(1):25-33. doi: 10.1055/s-2008-1040823. PMID: 10711986

Therapy

Soltanzadeh P
Genes (Basel) 2022 Feb 17;13(2) doi: 10.3390/genes13020367. PMID: 35205411Free PMC Article
Ait Benichou S, Jauvin D, De Serres-Bérard T, Pierre M, Ling KK, Bennett CF, Rigo F, Gourdon G, Chahine M, Puymirat J
Gene Ther 2022 Dec;29(12):698-709. Epub 2022 Jan 25 doi: 10.1038/s41434-022-00316-7. PMID: 35075265Free PMC Article
Marsh S, Hanson B, Wood MJA, Varela MA, Roberts TC
Mol Ther 2020 Dec 2;28(12):2527-2539. Epub 2020 Oct 14 doi: 10.1016/j.ymthe.2020.10.005. PMID: 33171139Free PMC Article
Kelly AM
Curr Opin Pulm Med 2009 Jul;15(4):376-9. doi: 10.1097/MCP.0b013e32832ae314. PMID: 19373088
Mai A
Expert Opin Ther Targets 2007 Jun;11(6):835-51. doi: 10.1517/14728222.11.6.835. PMID: 17504020

Prognosis

Meola G, Jones K, Wei C, Timchenko LT
Histol Histopathol 2013 Sep;28(9):1089-98. Epub 2013 Mar 28 doi: 10.14670/HH-28.1089. PMID: 23536431
Timman R, Tibben A, Wintzen AR
J Rehabil Med 2010 Oct;42(9):823-30. doi: 10.2340/16501977-0598. PMID: 20878042
Kelly AM
Curr Opin Pulm Med 2009 Jul;15(4):376-9. doi: 10.1097/MCP.0b013e32832ae314. PMID: 19373088
Lambrecht JT, Kreusch T
Cleft Palate Craniofac J 1997 Jul;34(4):342-50. doi: 10.1597/1545-1569_1997_034_0341_eyocpf_2.3.co_2. PMID: 9257026
Moore JK, Moore AP
Anaesthesia 1987 May;42(5):529-33. doi: 10.1111/j.1365-2044.1987.tb04047.x. PMID: 3592181

Clinical prediction guides

Di Leo V, Lawless C, Roussel MP, Gomes TB, Gorman GS, Russell OM, Tuppen HAL, Duchesne E, Vincent AE
J Neuromuscul Dis 2023;10(6):1111-1126. doi: 10.3233/JND-230099. PMID: 37638448Free PMC Article
Hamilton MJ, Atalaia A, McLean J, Cumming SA, Evans JJ, Ballantyne B, Jampana R, The Scottish Myotonic Dystrophy Consortium, Longman C, Livingston E, van der Plas E, Koscik T, Nopoulos P, Farrugia ME, Monckton DG
Neuromuscul Disord 2022 May;32(5):377-389. Epub 2022 Feb 14 doi: 10.1016/j.nmd.2022.02.003. PMID: 35361525
Ait Benichou S, Jauvin D, De Serres-Bérard T, Pierre M, Ling KK, Bennett CF, Rigo F, Gourdon G, Chahine M, Puymirat J
Gene Ther 2022 Dec;29(12):698-709. Epub 2022 Jan 25 doi: 10.1038/s41434-022-00316-7. PMID: 35075265Free PMC Article
Reigneau M, Pouaha J, Truchetet F
Eur J Dermatol 2013 Nov-Dec;23(6):882-4. doi: 10.1684/ejd.2013.2226. PMID: 24334244
Vainzof M, Ayub-Guerrieri D, Onofre PC, Martins PC, Lopes VF, Zilberztajn D, Maia LS, Sell K, Yamamoto LU
J Mol Neurosci 2008 Mar;34(3):241-8. Epub 2008 Jan 18 doi: 10.1007/s12031-007-9023-9. PMID: 18202836

Supplemental Content

Table of contents

    Clinical resources

    Practice guidelines

    • PubMed
      See practice and clinical guidelines in PubMed. The search results may include broader topics and may not capture all published guidelines. See the FAQ for details.

    Consumer resources

    Recent activity

    Your browsing activity is empty.

    Activity recording is turned off.

    Turn recording back on

    See more...