U.S. flag

An official website of the United States government

Format

Send to:

Choose Destination

Nephrotic syndrome, IIa 26(NPHS26)

MedGen UID:
1823994
Concept ID:
C5774221
Disease or Syndrome
Synonym: Nephrotic syndrome, type 26
 
Gene (location): LAMA5 (20q13.33)
 
Monarch Initiative: MONDO:0031061
OMIM®: 620049

Definition

Nephrotic syndrome type 26 (NPHS26) is an autosomal recessive renal disorder characterized by onset of proteinuria in the first months or years of life. Other features may include edema and hypoalbuminemia. Renal biopsy shows focal segmental glomerulosclerosis (FSGS), diffuse mesangial sclerosis (DMS), abnormalities of the glomerular basement membrane, and effacement of podocyte foot processes. There is variability in disease progression and response to treatment: some patients respond to steroids, whereas others show steroid resistance and progression to end-stage renal disease (ESRD) (Braun et al., 2019; Taniguchi et al., 2021). For a general phenotypic description and a discussion of genetic heterogeneity of nephrotic syndrome, see NPHS1 (256300). [from OMIM]

Clinical features

From HPO
Focal segmental glomerulosclerosis
MedGen UID:
4904
Concept ID:
C0017668
Disease or Syndrome
Segmental accumulation of scar tissue in individual (but not all) glomeruli.
Nephrotic syndrome
MedGen UID:
10308
Concept ID:
C0027726
Disease or Syndrome
Nephrotic syndrome is a collection of findings resulting from glomerular dysfunction with an increase in glomerular capillary wall permeability associated with pronounced proteinuria. Nephrotic syndrome refers to the constellation of clinical findings that result from severe renal loss of protein, with Proteinuria and hypoalbuminemia, edema, and hyperlipidemia.
Steroid-resistant nephrotic syndrome
MedGen UID:
588369
Concept ID:
C0403397
Disease or Syndrome
A form of nephrotic syndrome that does not respond to treatment with steroid medication, defined as persistent proteinuria despite 60mg/m2 or 2mg/kg for 8 weeks, after insuring no infection or non-adherence to medication.
Stage 5 chronic kidney disease
MedGen UID:
384526
Concept ID:
C2316810
Disease or Syndrome
A degree of kidney failure severe enough to require dialysis or kidney transplantation for survival characterized by a severe reduction in glomerular filtration rate (less than 15 ml/min/1.73 m2) and other manifestations including increased serum creatinine.

Recent clinical studies

Etiology

de Seigneux S, Courbebaisse M, Rutkowski JM, Wilhelm-Bals A, Metzger M, Khodo SN, Hasler U, Chehade H, Dizin E, Daryadel A, Stengel B; NephroTest Study Group, Girardin E, Prié D, Wagner CA, Scherer PE, Martin PY, Houillier P, Feraille E
J Am Soc Nephrol 2015 Jul;26(7):1608-18. Epub 2014 Oct 27 doi: 10.1681/ASN.2014010104. PMID: 25349200Free PMC Article

Diagnosis

de Seigneux S, Courbebaisse M, Rutkowski JM, Wilhelm-Bals A, Metzger M, Khodo SN, Hasler U, Chehade H, Dizin E, Daryadel A, Stengel B; NephroTest Study Group, Girardin E, Prié D, Wagner CA, Scherer PE, Martin PY, Houillier P, Feraille E
J Am Soc Nephrol 2015 Jul;26(7):1608-18. Epub 2014 Oct 27 doi: 10.1681/ASN.2014010104. PMID: 25349200Free PMC Article
Ongajyooth L, Sirisalee K, Laohaphand T, Parichatiganond P, Shayakul C, Nilwarangkur S
J Med Assoc Thai 1993 Sep;76(9):512-20. PMID: 7964258

Therapy

Fujita A, Tsukaguchi H, Koshimizu E, Nakazato H, Itoh K, Kuraoka S, Komohara Y, Shiina M, Nakamura S, Kitajima M, Tsurusaki Y, Miyatake S, Ogata K, Iijima K, Matsumoto N, Miyake N
Ann Neurol 2018 Dec;84(6):814-828. doi: 10.1002/ana.25370. PMID: 30427554
Mincu I, Ionescu-Tîrgoviste C, Stanescu J, Boboia D, Cheta D, Popa E, Mihalache N, Georgescu M
Diabete Metab 1976 Dec;2(4):171-82. PMID: 1017536

Prognosis

de Seigneux S, Courbebaisse M, Rutkowski JM, Wilhelm-Bals A, Metzger M, Khodo SN, Hasler U, Chehade H, Dizin E, Daryadel A, Stengel B; NephroTest Study Group, Girardin E, Prié D, Wagner CA, Scherer PE, Martin PY, Houillier P, Feraille E
J Am Soc Nephrol 2015 Jul;26(7):1608-18. Epub 2014 Oct 27 doi: 10.1681/ASN.2014010104. PMID: 25349200Free PMC Article

Clinical prediction guides

de Seigneux S, Courbebaisse M, Rutkowski JM, Wilhelm-Bals A, Metzger M, Khodo SN, Hasler U, Chehade H, Dizin E, Daryadel A, Stengel B; NephroTest Study Group, Girardin E, Prié D, Wagner CA, Scherer PE, Martin PY, Houillier P, Feraille E
J Am Soc Nephrol 2015 Jul;26(7):1608-18. Epub 2014 Oct 27 doi: 10.1681/ASN.2014010104. PMID: 25349200Free PMC Article

Supplemental Content

Recent activity

Your browsing activity is empty.

Activity recording is turned off.

Turn recording back on

See more...